Genetic Disorder Cluster Muscular Dystrophy Drug Development Pipeline Market Review, 2017

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Genetic Disorder Cluster Muscular Dystrophy Drug Development Pipeline Market Review, 2017

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Genetic Disorder Pipeline Muscular Dystrophy Market Review in 2017 Report provides an overview of the Genetic Disorder Clusters pipeline landscape. The Genetic Disorder Cluster market report provides comprehensive information on the therapeutics under development and key players involved in therapeutic development for Becker and Duchenne Muscular Dystrophy (BMD and DMD) and features dormant and discontinued projects. Both indications covered are inherited muscular dystrophies, a group of genetic, degenerative diseases primarily affecting voluntary muscles. To Get Discount on Report @ Goo.gle/Report . – PowerPoint PPT presentation

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Title: Genetic Disorder Cluster Muscular Dystrophy Drug Development Pipeline Market Review, 2017


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Genetic Disorder Cluster Muscular Dystrophy Drug
Development Pipeline Review, 2017
Order this report by calling 1 888 391 5441 or
Send an email to sales_at_reportsandreports.com with
your contact details and questions if any.
  • Published May 2017
  • Single User PDF US 3995

2
Genetic Disorder Cluster Muscular Dystrophy Drug
Development Pipeline Review, 2017
  • The Genetic Disorder Cluster Muscular Dystrophy
    Drug Development Pipeline report provides an
    overview of the genetic disorders pipeline
    landscape. It provides information on the
    therapeutics under development and key players
    involved in therapeutic development for Becker
    and Duchenne Muscular Dystrophy (BMD and DMD) and
    features dormant and discontinued projects. Both
    indications covered are inherited muscular
    dystrophies, a group of genetic, degenerative
    diseases primarily affecting voluntary muscles.
  • BMD, the first type of muscular dystrophy, leads
    to symptoms include pain and sensation,
    difficulty with running, hopping, and jumping,
    toe walking, breathing problems, cognitive
    problems and frequent falls. There are a total of
    six products in development for this indication,
    by six separate companies.
  • Access Complete Report at http//www.reportsnrepo
    rts.com/reports/1001382-genetic-disorder-cluster-m
    uscular-dystrophy-drug-development-pipeline-review
    -2017.html.
  • Offers from 10th May 2017 to 2nd June 2017
  • All reports priced gt1,000 20 Discount
    Single User 25 Discount Global Site License.
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3
Genetic Disorder Cluster Muscular Dystrophy Drug
Development Pipeline Review, 2017
  • DMD is a condition which causes muscle weakness,
    and is an X-linked disorder. The gene for DMD is
    present on the X chromosome. It codes for a
    protein named dystrophin. Dystrophin is essential
    for providing structural support inside muscle
    cells.
  • Symptoms usually appear before age 6 and may
    appear as early as infancy. They include fatigue,
    learning difficulties, intellectual disability,
    muscle weakness and progressive difficulty
    walking.
  • Key companies operating in this pipeline space
    include Sarepta Therapeutics, PTC Therapeutics,
    WAVE Life Sciences, Solid Biosciences, Summit
    Therapeutics and Catabasis Pharmaceuticals. Of
    particular importance are Sarepta, who are
    developing twelve distinct pipeline products for
    DMD. As with BMD, these are all smaller
    enterprises, although there is some involvement
    from larger pharmaceutical companies such as
    Pfizer and Merck in the DMD pipeline.
  • There is a far larger pipeline for DMD than for
    BMD there are a total of 108 products in
    development for DMD, by 57 companies and nine
    academic institutions.
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    m/contacts/discount.aspx?name1001382.

Order this report by calling 1 888 391 5441 or
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4
Genetic Disorder Cluster Muscular Dystrophy Drug
Development Pipeline Review, 2017
  • Key Companies Operating in this Pipeline include
  • The companies operating in this pipeline space
    are all small pharmaceutical enterprises, and
    consist of Armgo Pharma, Cardero Therapeutics,
    Milo Biotechnology, PTC Therapeutics, ReveraGen
    BioPharma and Sarepta Therapeutics.
  • The majority of pipeline products for DMD target
    dystrophin which, as mentioned, is the causative
    gene for the disease. However, a number of
    products act on other molecular targets such as
    growth differentiation factor 8, nuclear factor
    kappa B and utrophin. The first two of these make
    up the pipeline for BMD, along with fork head box
    protein 1B.
  • Buy a Copy of Report _at_ http//www.reportsnreports.
    com/purchase.aspx?name1001382.

Order this report by calling 1 888 391 5441 or
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5
Genetic Disorder Cluster Muscular Dystrophy Drug
Development Pipeline Review, 2017
  • Scope of the Report
  • Which companies are the most active within the
    pipeline for genetic disorder therapeutics?
  • Which pharmaceutical approaches are the most
    prominent at each stage of the pipeline and
    within each indication?
  • To what extent do universities and institutions
    play a role within this pipeline, compared to
    pharmaceutical companies?
  • What are the most important RD milestones and
    data publications to have happened in the field
    of genetic disorder therapeutics?
  • Buy a Copy of Report _at_ http//www.reportsnreports.
    com/purchase.aspx?name1001382.

Order this report by calling 1 888 391 5441 or
Send an email to sales_at_reportsandreports.com with
your contact details and questions if any.
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